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  • Single-Dose Gene-Replacemen...
    Mendell, Jerry R.; Al-Zaidy, Samiah; Shell, Richard; Arnold, W. Dave; Rodino-Klapac, Louise R.; Prior, Thomas W.; Lowes, Linda; Alfano, Lindsay; Berry, Katherine; Church, Kathleen; Kissel, John T.; Nagendran, Sukumar; L’Italien, James; Sproule, Douglas M.; Wells, Courtney; Cardenas, Jessica A.; Heitzer, Marjet D.; Kaspar, Allan; Corcoran, Sarah; Braun, Lyndsey; Likhite, Shibi; Miranda, Carlos; Meyer, Kathrin; Foust, K.D.; Burghes, Arthur H.M.; Kaspar, Brian K.

    The New England journal of medicine, 11/2017, Letnik: 377, Številka: 18
    Journal Article