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  • Efficacy and Safety of Vamorolone Over 48 Weeks in Boys With Duchenne Muscular Dystrophy: A Randomized Controlled Trial
    Dang, Utkarsh J; Damsker, Jesse M; Guglieri, Michela ... Neurology, 2024-Mar-12, Letnik: 102, Številka: 5
    Journal Article
    Recenzirano

    Vamorolone is a dissociative agonist of the glucocorticoid receptor that has shown similar efficacy and reduced safety concerns in comparison with prednisone in Duchenne muscular dystrophy (DMD). ...
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